National Award Recognizes Commitment to Positive Impact and Transparency

Linda Howard, Daniel Klein, and John Rushing Join The Assistance Fund’s Board of Directors

"Rare" is a film exploring the world of rare diseases and the unsung heroes pushing for medical breakthroughs.

Across Rare Diseases, Neuroscience/Mental Health, Immunology and Gastroenterology

1,000 patients will receive free whole genome sequencing and interpretation, including personalized reports, thanks to Epilepsy Awareness Day at Disneyland, in a push to advance new research and gene therapies

Nancy Alexander, Account Director, Southeast at Sanofi Genzyme, joins networking organization

Alongside You at Rare Finds YVR event

SOM Biotech has launched a crowdfunding campaign to raise funds for five new early-stage R&D projects in pediatric rare diseases. These diseases are Cystic Fibrosis, Duchenne Muscular Dystrophy, Gaucher Disease, Niemann Pick Disease Type C, and Osteogenesis Imperfecta (Brittle Bones Disease). This ambitious move comes in light of growing optimism of its current clinical programs. SOM Biotech seeks to raise at least 300,000 USD$ in donations within a 2-month period.

As part of its global campaign to raise awareness for rare diseases and the Americans afflicted by them, the FDA has highlighted Epidermolysis Bullosa (EB) and the Jackson Gabriel Silver Foundation. JGSF founder Alexander Silver said "We're honor